Researchers report that all nine patients who were successfully treated for ADA-SCID in a UCLA clinical trial from 2009 to 2012 are still disease-free.
Research brief: Scientists have identified hundreds of chemical modifications that can alter RNA’s protein-making instructions without affecting the core DNA.
Research brief: A UCLA team has demonstrated that altering a key molecule used in the therapy yields superior and longer-lasting results in mouse models.
Research brief: An approach pioneered at UCLA predicts which methicillin-resistant Staphylococcus aureus infections are likely to be cured with antibiotic therapy.